Rescuing Phenotypes in PTHS-Derived Brain Organoids with Alysson Muotri - Sanford Stem Cell Symposium 2022

11/28/2022; 18 minutes

Alysson Muotri discusses modeling Pitt-Hopkins syndrome (PTHS) using stem cells and brain organoids. He shares how rescuing TCF4 expression with CRISPR-mediated epigenetic induction of AAV vector delivery provides a gateway for targeted therapeutics for PTHS and related conditions. (#38516)

Like what you learn?

Donate to UCTV to support informative & inspiring programming.

Links & Resources

More Programs With

Explore more in this series:
Sanford Stem Cell Symposium 2022
Sanford Stem Cell Symposium 2022
 
 

SIGN UP FOR EMAIL UPDATES
Subscribe to receive email notifications about featured videos.
(c)2020 Regents of the University of California. All right reserved. Terms and Conditions of Use.